Early Intervention with Intravenous AAV9 Gene Therapy Significantly Improves Biomarkers and Phenotypes in a Floxed Mouse Model of X-linked Alport Syndrome
Authors: Hiroyuki Nakai, Ranjan Das, Taisuke Furusho, Anusha Sairavi, Hideyuki Hakui, Shuhua Luo, Lena Li, Jeffrey H. Miner