Ocular Gene Therapy in a Patient with Dystrophic Epidermolysis Bullosa

Authors: Arianna Tovar Vetencourt, Ibrahim Sayed-Ahmed, Jennifer Gomez, Hubert Chen, Brittani Agostini, Kate Carroll, Trevor Parry, Suma Krishnan, Alfonso L. Sabater

Published: 2024-02-07

DOI: 10.1056/nejmoa2301244

Source: Full article


Abstract

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