Oral Iptacopan Monotherapy in Paroxysmal Nocturnal Hemoglobinuria

Authors: Régis Peffault de Latour, Alexander Röth, Austin G. Kulasekararaj, Bing Han, Phillip Scheinberg, Jaroslaw P. Maciejewski, Yasutaka Ueda, Carlos M. de Castro, Eros Di Bona, Rong Fu, Li Zhang, Morag Griffin, Saskia M.C. Langemeijer, Jens Panse, Hubert Schrezenmeier, Wilma Barcellini, Vitor A.Q. Mauad, Philippe Schafhausen, Suzanne Tavitian, Eloise Beggiato, Lee Ping Chew, Anna Gaya, Wei-Han Huang, Jun Ho Jang, Toshio Kitawaki, Abdullah Kutlar, Rosario Notaro, Vinod Pullarkat, Jörg Schubert, Louis Terriou, Michihiro Uchiyama, Lily Wong Lee Lee, Eng-Soo Yap, Flore Sicre de Fontbrune, Luana Marano, Ferras Alashkar, Shreyans Gandhi, Roochi Trikha, Chen Yang, Hui Liu, Richard J. Kelly, Britta Höchsmann, Cécile Kerloeguen, Partha Banerjee, Rafael Levitch, Rakesh Kumar, Zhixin Wang, Christine Thorburn, Samopriyo Maitra, Shujie Li, Aurelie Verles, Marion Dahlke, Antonio M. Risitano

Published: 2024-03-13

DOI: 10.1056/nejmoa2308695

Source: Full article


Abstract

No abstract found.