Transcriptional adaptation upregulates utrophin in Duchenne muscular dystrophy

Authors: Lara Falcucci, Christopher M. Dooley, Douglas Adamoski, Thomas Juan, Justin Martinez, Angelina M. Georgieva, Kamel Mamchaoui, Cansu Cirzi, Didier Y. R. Stainier

Published: 2025-02-12

DOI: 10.1038/s41586-024-08539-x

Source: Full article


Abstract

Abstract