In vivo base editing extends lifespan of a humanized mouse model of prion disease

Authors: Meirui An, Jessie R. Davis, Jonathan M. Levy, Fiona E. Serack, John W. Harvey, Pamela P. Brauer, Catherine P. Pirtle, Kiara N. BerrĂ­os, Gregory A. Newby, Wei-Hsi Yeh, Nikita Kamath, Meredith Mortberg, Yuan Lian, Michael Howard, Kendrick DeSouza-Lenz, Kenia Guzman, Aaron Thai, Samantha Graffam, Vanessa Laversenne, Alissa A. Coffey, Jeannine Frei, Sarah E. Pierce, Jiri G. Safar, Benjamin E. Deverman, Eric Vallabh Minikel, Sonia M. Vallabh, David R. Liu

Published: 2025-01-14

DOI: 10.1038/s41591-024-03466-w

Source: Full article


Abstract

Abstract