Gene Therapy with Fidanacogene Elaparvovec in Adults with Hemophilia B

Authors: Adam Cuker, Kaan Kavakli, Laurent Frenzel, Jiaan-Der Wang, Jan Astermark, Monica H. Cerqueira, Alfonso Iorio, Olga Katsarou-Fasouli, Robert Klamroth, Amy D. Shapiro, Cédric Hermans, Akira Ishiguro, Andrew D. Leavitt, Johannes B. Oldenburg, Margareth C. Ozelo, Jerome Teitel, Francesca Biondo, Annie Fang, Joanne Fuiman, John McKay, Pengling Sun, John E.J. Rasko, Jeremy Rupon

Published: 2024-09-25

DOI: 10.1056/nejmoa2302982

Source: Full article


Abstract

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