Efanesoctocog Alfa Prophylaxis for Children with Severe Hemophilia A

Authors: Lynn Malec, Flora Peyvandi, Anthony K.C. Chan, Christoph Königs, Bulent Zulfikar, Huixing Yuan, Mindy Simpson, Maria Teresa Álvarez Román, Manuel Carcao, Janice M. Staber, Amy L. Dunn, Sheng-Chieh Chou, Roseline d’Oiron, Manuela Albisetti, Marek Demissie, Elena Santagostino, Abhimanyu Yarramaneni, Nancy Wong, Lydia Abad-Franch, Sriya Gunawardena, Karin Fijnvandraat

Published: 2024-07-17

DOI: 10.1056/nejmoa2312611

Source: Full article


Abstract

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