CRISPR-Based Therapy for Hereditary Angioedema

Authors: Danny M. Cohn, Padmalal Gurugama, Markus Magerl, Constance H. Katelaris, David Launay, Laurence Bouillet, Remy S. Petersen, Karen Lindsay, Emel Aygören-Pürsün, David Maag, James S. Butler, Mrinal Y. Shah, Adele Golden, Yuanxin Xu, Ahmed M. Abdelhady, David Lebwohl, Hilary J. Longhurst

Published: 2024-10-24

DOI: 10.1056/nejmoa2405734

Source: Full article


Abstract

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