Ethical Drug Development for Rare Childhood Diseases: When There Are Limited But Promising Data in Adults, How to Choose Between Safety or Efficacy Studies?

Authors: Liza-Marie Johnson, Devan M. Duenas, Benjamin S. Wilfond

Published: 2020-03-24

DOI: 10.1080/15265161.2020.1730490

Source: Full article


Abstract

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