Abstract 10727: Results from First-in-Human Clinical Trial of RP-A501 (AAV9:LAMP2B) Gene Therapy Treatment for Danon Disease

Authors: Barry Greenberg, Emily Eshraghian, Pavan Battiprolu, David Ricks, Paul Yarabe, Jonathan Schwartz, Kinnari Patel, Guarav Shah, Jose Trevejo

Published: 2022-03-19

DOI: 10.1161/circ.144.suppl_1.10727

Source: Full article

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Abstract

Background: