Synthesis, Biophysical and Biological Evaluation of Splice-Switching Oligonucleotides with Multiple LNA-Phosphothiotriester Backbones

Authors: Debashis Dhara, Alyssa C. Hill, Abinaya Ramesh, Matthew J. A. Wood, Afaf H. El-Sagheer, Tom Brown

Published: 2024-10-14

DOI: 10.1021/jacs.4c11402

Source: Full article


Abstract

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