Engineered PsCas9 enables therapeutic genome editing in mouse liver with lipid nanoparticles

Authors: Dmitrii Degtev, Jack Bravo, Aikaterini Emmanouilidi, Aleksandar Zdravković, Oi Kuan Choong, Julia Liz Touza, Niklas Selfjord, Isabel Weisheit, Margherita Francescatto, Pinar Akcakaya, Michelle Porritt, Marcello Maresca, David Taylor, Grzegorz Sienski

Published: 2024-11-07

DOI: 10.1038/s41467-024-53418-8

Source: Full article


Abstract

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