A novel AAV Vector for gene therapy of RPE-related retinal degenerative diseases via intravitreal delivery

Authors: Yajun Gong, Xianyu Huang, Tianxiang Tu, Cenfeng Chu, Chunrui Xian, Yushun Yuan, Xin Fu, Ruobi Li, Guisheng Zhong, Xiaolai Zhou

Published: 2024-11-25

DOI: 10.1186/s13024-024-00777-x

Source: Full article


Abstract

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