Phase 1–2 Trial of Antisense Oligonucleotide Tofersen for

Authors: Timothy Miller, Merit Cudkowicz, Pamela J. Shaw, Peter M. Andersen, Nazem Atassi, Robert C. Bucelli, Angela Genge, Jonathan Glass, Shafeeq Ladha, Albert L. Ludolph, Nicholas J. Maragakis, Christopher J. McDermott, Alan Pestronk, John Ravits, François Salachas, Randall Trudell, Philip Van Damme, Lorne Zinman, C. Frank Bennett, Roger Lane, Alfred Sandrock, Heiko Runz, Danielle Graham, Hani Houshyar, Alexander McCampbell, Ivan Nestorov, Ih Chang, Manjit McNeill, Laura Fanning, Stephanie Fradette, Toby A. Ferguson

Published: 2020-07-08

DOI: 10.1056/nejmoa2003715

Source: Full article


Abstract

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