PS1527 HYDROXYUREA ESCALATED TO MAXIMAL TOLERATED DOSE IN CHILDREN WITH SICKLE CELL ANEMIA AND BCL11A: BENEFITS FOR END-ORGAN DAMAGE AND ACUTE COMPLICATIONS UP TO 6 YEARS OF AGE
Authors: J.H. Estepp, W. Wang, H. Li, S. Hwang, J. Hodges, M. Villavicencio, M. Smeltzer, M. Weiss, G. Kang, J. Hankins