SLN124, a GalNAc-siRNA Conjugate Targeting TMPRSS6, Efficiently Prevents Iron Overload in Hereditary Haemochromatosis Type 1

Authors: Sandro Altamura, Ute Schaeper, Sibylle Dames, Kathrin Löffler, Mona Eisermann, Christian Frauendorf, Katja Müdder, Joana Neves, Martina U. Muckenthaler

Published: 2019-10-28

DOI: 10.1097/hs9.0000000000000301

Source: Full article


Abstract

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