CRISPR-Cas12a delivery by DNA-mediated bioresponsive editing for cholesterol regulation

Authors: Wujin Sun, Jinqiang Wang, Quanyin Hu, Xingwu Zhou, Ali Khademhosseini, Zhen Gu

Published: 2020-05-20

DOI: 10.1126/sciadv.aba2983

Source: Full article


Abstract

A DNA-based bioresponsive nanoformulation delivers the CRISPR-Cas12a to hepatocytes for regulating serum cholesterol.