Pharmacological enhancement of

Authors: Xin Tang, Jesse Drotar, Keji Li, Cullen D. Clairmont, Anna Sophie Brumm, Austin J. Sullins, Hao Wu, Xiaoxiao Shawn Liu, Jinhua Wang, Nathanael S. Gray, Mriganka Sur, Rudolf Jaenisch

Published: 2019-07-31

DOI: 10.1126/scitranslmed.aau0164

Source: Full article


Abstract

KCC2 expression–enhancing small molecules rescue cellular and behavior deficits in human RTT neurons and