EPCT-16. A PHASE IB STUDY OF PTC596 IN CHILDREN WITH NEWLY DIAGNOSED DIFFUSE INTRINSIC PONTINE GLIOMA AND HIGH GRADE GLIOMA

Authors: Natasha Pillay Smiley, Patricia Baxter, Shiva Kumar, Eugene Hwang, John Breneman, Adam Lane, Renee Doughman, Michelle Deutsch, Charles Stevenson, Clinton Stewart, Jim Leach, Xiao-Nan Li, Sonia Romero, Pius Maliakal, Lan Gao, Maryam Fouladi, Rachid Drissi

Published: 2020-12-04

DOI: 10.1093/neuonc/noaa222.138

Source: Full article


Abstract

Abstract