P104: BASE EDITING REPAIRS THE HBE MUTATION RESTORING THE PRODUCTION OF NORMAL GLOBIN CHAINS IN SEVERE HBE/β-THALASSEMIA PATIENT HEMATOPOIETIC STEM AND ERYTHROID CELLS
Authors: M Badat, P Hua, S Mettananda, C Fisher, N Roy, S Rice, A Roy, D Higgs, J Davies