S101: COMBINATION OF A LUSPATERCEPT-LIKE DRUG (RAP-GRL) AND TMPRSS6-ASO IS SUPERIOR TO EITHER DRUG ALONE FOR CORRECTING β-THALASSEMIA

Authors: A. Guerra, P. Demsko, S. Sinha, P. McVeigh, C. Castruccio Castracani, L. Breda, C. Casu, S. Rivella

Published: 2022-01-31

DOI: 10.1097/hs9.0000000000000684

Source: Full article


Abstract

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