Secreted acid sphingomyelinase as a potential gene therapy for limb girdle muscular dystrophy 2B

Authors: Daniel C. Bittel, Sen Chandra Sreetama, Goutam Chandra, Robin Ziegler, Kanneboyina Nagaraju, Jack H. Van der Meulen, Jyoti K. Jaiswal

Published: 2022-01-03

DOI: 10.1172/jci141295

Source: Full article


Abstract

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