A phase I/II study on intracerebroventricular tralesinidase alfa in patients with Sanfilippo syndrome type B

Authors: Nicole Muschol, Anja Koehn, Katharina von Cossel, Ilyas Okur, Fatih Ezgu, Paul Harmatz, Maria J. de Castro Lopez, Maria Luz Couce, Shuan-Pei Lin, Spyros Batzios, Maureen Cleary, Martha Solano, Igor Nestrasil, Brian Kaufman, Adam J. Shaywitz, Stephen M. Maricich, Bernice Kuca, Joseph Kovalchin, Eric Zanelli

Published: 2022-11-22

DOI: 10.1172/jci165076

Source: Full article

---

Abstract

No abstract found.