P754: PRIME EDITING AS A NOVEL TOOL FOR PRECISE CORRECTION OF CAUSAL MUTATIONS IN FANCONI ANAEMIA GROUP A PATIENT-DERIVED CELLS

Authors: Lucie Peterkova, Markéta Racková, Michael Svaton, Petr Riha, Drahuse Novotna, Petr Sedlacek, Lucie Sramkova, Karolina Skvarova

Published: 2023-08-08

DOI: 10.1097/01.hs9.0000969920.27248.b5

Source: Full article


Abstract

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