PB2063: APPULSE-PNH: A PHASE IIIB TRIAL TO EVALUATE THE EFFICACY AND SAFETY OF SWITCHING TO IPTACOPAN IN PATIENTS WITH PAROXYSMAL NOCTURNAL HEMOGLOBINURIA (PNH) ON ANTI-C5 THERAPY WITH HEMOGLOBIN >10G/DL

Authors: Antonio Maria Risitano, David J Araten, David Kuter, Bhumika J Patel, Régis Peffault de Latour, Marion Dahlke, Tania Garito, Shujie LI, Samopriyo Maitra, Austin Kulasekararaj

Published: 2023-08-09

DOI: 10.1097/01.hs9.0000975052.08587.b7

Source: Full article


Abstract

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