New opportunities for accessing promising non-oncological orphan drugs

Authors: Carla E.M. Hollak, Carelle C. Reparon-Schuijt, Kathelijn Verdeyen, Lisa J. Deesker, Jaap W. Groothoff, Josephine M.I. Vos, Atse H. Huisman, Silvia van der Flier, Anke A.M.G. Pisters-van Roy

Published: 2025-03-22

DOI: 10.1016/j.lanepe.2025.101275

Source: Full article


Abstract

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