Long-term efficacy and safety of mRNA therapy in two murine models of methylmalonic acidemia

Authors: Ding An, Andrea Frassetto, Eric Jacquinet, Marianne Eybye, Joseph Milano, Christine DeAntonis, Vi Nguyen, Rodrigo Laureano, Jaclyn Milton, Staci Sabnis, Christine M. Lukacs, Lin T. Guey

Published: 2019-07-12

DOI: 10.1016/j.ebiom.2019.07.003

Source: Full article


Abstract

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